Question

What term describes the normal genes that are inserted into an individual's diseased cells in gene therapy? Describe three ways these genes can be inserted.

Answer 1

Human Gene Therapy.

(It is all of these)

A. includes the insertion of genetic material into human cells for the treatment of a genetic disease.

B. Has been used for treatment of children who have severe combined immunodeficiency.

C. Has been used in a trial to treat familial hypercholesterolemia.

Can be injected by IV, shots that go into the vein to carry the gene all the way around the human body system, and possibly pills (possibly).