Question

Cystic fibrosis is a devastating illness that affects the lungs, pancreas, and intestines.In 1989, researchers discovered that the disease is caused by a mutation in a gene that produces a proteinthat channels chloride across cellular membranes. People with two copies (or alleles) of the mutated genehave a buildup of mucus in the airways, intestines, and other organs due to nonfunctioning or absent channelproteins. Suggest two ways you could intervene to treat the disease by targeting the DNA molecule and justifywhy each approach could be effective.Student answers will vary, but answers should

Answer 1

There is no cure for cystic fibrosis, but treatment can ease symptoms and reduce complications.

Step-by-step explanation:

1). For those with cystic fibrosis who have certain gene mutations, doctors may recommend a newer medication called ivacaftor. This medication may improve lung function and weight, increases the activity of Cystic fibrosis transmembrane conductance regulator (CFTR)protein and reduce the amount of salt in sweat. It has been approved by the Food and Drug Administration for people with cystic fibrosis who are age 6 and older. The dose depends on your weight and age.

2). For people with a certain gene mutation who are age 12 and older, another drug is available that combines ivacaftor with a medication called lumacaftor. This drug is called orkambi.

The use of Orkambi may improve lung function and reduce the risk of exacerbations.

I hope you're clear on this Daxxy